Reaching Rare Disease and Pediatric Patients
In a population with underserved and unmet needs, developing targeted therapies for these conditions is not only essential, but also urgent. That’s why PPD has been committed to serving these patients for so long. We established a Rare Disease and Pediatric Center of Excellence well before rare diseases became a focal point for the industry. We continue to maintain our deep commitment to advancing rare disease research across the globe.”
ppd’s EXPERIENCE in the past five years:
The Care Ecosystem
The challenges of developing rare disease therapies are numerous and include the need to engage research-naïve sites and access small, widely dispersed patient populations.
We field direct input from patients, providers and caregivers to understand the patient burden of a disease and determine feasible therapeutic regimens. This early assessment of the patient’s care environment guides study and protocol design, while also positioning your clinical research program as a worthy care option – not as an obstacle along the way to a promising therapy.
We work with rare disease research organizations and advocacy groups while also connecting directly with physicians to identify patients.
RARE DISEASE AND PEDIATRIC CENTER OF EXCELLENCE
Our Rare Disease and Pediatric Center of Excellence team provides tailored thought leadership and innovation in the design and execution of trials, as well as aligned oversight of program delivery.
Our team of more than 20 rare disease experts from across the organization brings a wealth of experience across all therapeutic areas to provide strategic insights that inform and optimize clinical and regulatory strategy development.