Rare Disease Archives | PPD

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Young smiling female doctor and a child female patient with a teddy bear

Young smiling female doctor and a child female patient with a teddy bear

Overcoming Orphan Drug Development Challenges with Real-World Data and Evidence

Older male doctor examining young girl patient, while her mom listens in, smiling

Older male doctor examining young girl patient, while her mom listens in, smiling

Five Strategies to Tailor Your Pediatric Clinical Trials to the Child’s Needs

Pediatric doctor visiting young girl in hospital dad with dad smiling in the background

Pediatric doctor visiting young girl in hospital dad with dad smiling in the background

Three Ways Patients and Advocates Can Inform Rare Disease Trials

Woman in a field.

Woman in a field.

PPD Heroes: Advocating for the Patient’s Voice During COVID-19

Cell and Gene Therapy Lesson 5: Lab Concierge – Extreme Focus on the Rare Disease Patient and Precious Study Sample Logistics Through an Innovative Lab Concierge Program

a doctor and her patient reviewing test results

a doctor and her patient reviewing test results

Rare Disease Research: The Benefit of Registries

doctor going over paperwork with his patient

doctor going over paperwork with his patient

What’s on the Horizon for Oncology?

illustration of puzzle pieces and dna strands

illustration of puzzle pieces and dna strands

Natural History Studies in Rare Diseases and Genetic Biomarkers

meeting

meeting

Patient Engagement in Clinical Trial Protocol Design and Recruitment Strategies

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