mother and child talking to doctor about rare neurological disorder

Rare Neurological Disorders

Committed to rare neurological disease research

Creating treatments and executing complex clinical trials for rare neurological disorders requires the expertise and support of an experienced team with a broad range of skills. It’s important to partner with a CRO that enables you to manage the challenges of treating rare neurological diseases with specialized and flexible development strategies that incorporate rigorous feasibility assessment, robust training, and supportive site-network relationships with patient advocacy group collaboration and concierge services.

Prioritizing the patient experience is key to achieving your rare neurological trial’s goals. Adopting a patient-centric approach keeps the patients’ needs top of mind and proactively helps them navigate the complexities of participating in clinical trials. Not only does this approach help with recruitment and increase retention in trials — it also ensures that the humanity of every patient is prioritized during a difficult time in their lives. Prioritize the patient experience of your clinical trial with PPD’s customizable patient concierge offerings.

Accelerate your gene therapy trial

Gene therapies are changing outcomes for rare neurological diseases. We create streamlined gene therapy study protocols and designs to help you meet your goals effectively.

Move your trial forward

Finding a cure for patients living with rare neurological disorders like amyotrophic lateral sclerosis (ALS)and Duchenne muscular dystrophy is crucial to you, and we share your determination. Despite the many complexities inherent to developing treatments for these and other related conditions, these trials are an opportunity to transform the lives of millions of patients. Together, we ensure your clinical trial is conscientious of the necessities of patient care and also meets rigorous global standards that are appropriate for a dispersed trial population.

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