Unlocking success: Overcoming cell & gene therapy challenges with real-world evidence
Rapid advancements in cell and gene therapy (CGT) are revolutionizing treatment, offering potential cures for previously untreatable conditions. However, the journey from development to market uptake is fraught with complex challenges and success is not guaranteed.
This webinar delves into critical issues in CGT development planning, exploring regulatory hurdles, new EU HTA and US IRA regulations, payer acceptance, and provider and patient uptake barriers. Hear actionable solutions supported by real-world evidence (RWE) and real-world data (RWD). Gain strategic insights that will help you navigate the intricate path of CGT development, ensuring successful regulatory approval and market penetration, and hear insights from Richard Diaz, a NICE guest panelist.
Learning objectives
- Understand how the changing regulatory environment (including EUHTAR and US IRA) is impacting CGT development and ways to plan strategically to address it
- Explore uptake issues, including regulatory, HTA, payer, provider, prescriber, and patient hurdles
- Learn about the applications of real-world data and evidence to the challenges of cell and gene therapy development and uptake
Panelists
Special guest panelist
Richard Diaz, BS
Associate Director – Medicines Evaluation, Rare Diseases, NICE, Manchester, England, United Kingdom
View other panelists
Pedro Saramago Goncalves, MSc, PhD
Research Scientist, Consulting, PPD Evidera Health Economics and Market Access, Thermo Fisher Scientific, London, England, United Kingdom
Martin Parkinson, MRPharmS
Executive Director, Consulting, PPD Evidera Health Economics and Market Access, Thermo Fisher Scientific, London, England, United Kingdom
Amanda Pulfer, BA
Executive Director, Integrated Solutions, RWE, PPD Evidera Real-World Data & Scientific Solutions, Thermo Fisher Scientific, London, England, United Kingdom
Heather Gelhorn, PhD
Vice President, Science, PPD Evidera Patient-Centered Research, Thermo Fisher Scientific, Waltham, MA, USA