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Boston, MA
All Events

Gene Therapy for Rare Disorders

  • Start Date:

    22 Feb 2021

  • End Date:

    25 Feb 2021

  • Location:

    Virtual Conference

  • Region:

    North America

Visit the conference website
request to meet with PPD

learn about our integrated cell and gene therapy development services from pre-clinical to post-approval

CLICK HERE FOR MORE INFORMATION>

PANEL

Evaluating Challenges Encountered in Small Patient Number Trials

Tuesday, February 23, 2021 | 3:00pm EST

Panelist: Tim Miller, MD, VP & Global Therapeutic Area Head, Lead, Rare Diseases & Pediatrics Center of Excellence, Medical and Scientific Strategy, PPD

Timothy Miller

Real-world Assessment of Commercialization Strategies for Rare Disease Gene Therapies

Wednesday, February 24, 2021 | 11:00am EST

Speaker: Raj Stewart, Senior Director, Consulting

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