PPD’s Rare Disease and Pediatric Center of Excellence is an experienced and dedicated cross-functional leadership team with clear accountabilities. The center of excellence team addresses strategic, operational, medical and scientific challenges presented by the small, widely dispersed patient populations that characterize rare diseases. A best-of-both-worlds solution, the center of excellence combines the traits of a niche contract research organization (CRO) with PPD’s global experience and focus on three key pillars:
Cutting-edge clinical development and regulatory strategy
Operational excellence and best practices
Innovation in patient access and patient experience
The center of excellence combines the traits of a niche CRO with PPD’s global footprint, infrastructure and experience.
The center of excellence team drives all rare disease and pediatric activities with accountabilities that span all therapeutic areas. The team provides tailored thought leadership and innovation in the design and execution of trials, as well as aligned oversight of program delivery and clear escalation paths for operational teams. In addition, the team provides strategic insights that can inform and optimize clinical and regulatory strategy development and facilitate access to a broad array of key stakeholders, including medical experts, patients and patient advocacy groups. Our team brings a wealth of experience combined with access to data, analytics and innovative technology solutions to advance and optimize the design and delivery of complex global programs in low prevalence indications.